Pipeline
Our AI workbench is enabling the discovery of novel therapeutic targets for diseases with high unmet need.
THERAPEUTIC AREA TARGET VALIDATION DISCOVERY PRECLINICAL CLINICAL PARTNER
CNS
Frontotemporal Dementia
Niemann-Pick Disease Type C
Pediatric Epilepsy
Parkinson's Disease
Metabolic
Wilson Disease
Refractory Gout
Partnered
Undisclosed
Undisclosed
Undisclosed
Undisclosed
Target Identification
Under Assessment (N=20)