Pipeline
Our AI workbench is enabling the discovery of novel therapeutic targets for diseases with high unmet need.
Target Discovery Preclinical Phase 1/2 Phase 3/Registration
Metabolic
Wilson Disease
DG12P1 ATP7B M645R
ATP7B SNV1
ATP7B SNV2
ATP7B SNV3
Undisclosed Metabolic
DG11P1 SNV1
Ophthalmologic
Undisclosed Retinopathy
SNV1
SNV2
SNV3